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Results from a phase 1 study of nusinersen (ISIS-SMNRx) in children with spinal muscular (...)
http://duke.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMwpV1ta9swEBZZC2Mwxt7Ysjc02EpLMLX8KkPp6NKEtUtTlhe6fTKWrRBvmRPsZl3_337YTpYUJ0vpOpYPJrEtBfse6XSn5-4QemMTj_ncDwyLcNNwHOYalLnEYK7LuM1c7pUZb87o8RfrU4-2m7XaLx0LU3KZhX1eqKFyRZSDiFcV_MZLXWHqXao21oV_ySSHw4-tEGzfwdYPkOzSbxC6HoFbb-32_-IFzgFiRPztP2Bm0SmcgO-AHDgCduB4I_T0eDGfnBcy-iRqzMag7BpEJqOV3A_Bl4fXl5VL1P5R3-ifdIU7ApRZIFwNgt--HCjeKGZlAa7vc0V9FU54nSv7q84hNc9X3PzNcZqnTDl_m5NoDmiuvK_9iymbJpEmheSXWbXJdRjluYxVex8V6aTigh9FWRbF8TSrSEnqovJ9EK8kf8npmqv52vIMzy4rsi8mdJVbWwHXXJqeqSxNqjW9ZAavKRHQ5iCfs25HJrdUH1gHuZXS1ESB7mnYHnY64aD1eXALbVpiwbWBNg-Om53TxW6Wa_mBCtuEvnev6nl1WbRm66xTdu9eTAWdovhWRlMsrYkG99E9ZczgA4mfB6jGs4fo9omiazxCqYIRFjDCES5hhAkuYYSnI1zBCG9rEG33fu7s4DTDGj5YwAfvjfclgrBGEFYI2tsd7z9Gw3Zr0PxgqNoeRuwEpmvEsK5MIpO5ceL5luOanDDqECcujXaPJtRKYrAmHJ-NKPMSz44djwcxd_2AsoDZTxFmCY8Dajs8oYnj8hHjzBrRhInmHCzzOrL1Ow1jlfFeFF6ZhMLyBUmEIInwT0nUkbFoNZMZX_5y_2strhCmZrHfFmV8Oi9C4vtgHoDFZF1zDzWpb3s0gH6eSBEv_tXyRNQ4IXXkrwh_cYNIDb96JUvHZYp4B3BIREuyApNQBldf-zzPbvA8z9Gdaji-QBvn-Zy_lOVUXinw_wYMs-S5
Neurology, Volume 86, Issue 10, pp. 890 - 897
Journal Article : Full Text Online
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Spinal muscular atrophy — insights and challenges in the treatment era
http://duke.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMwrV3db9MwELc2JiFe-BYURjESEg9g0sR27UhjqEytBhIdDBDwZMUf0R6gjZb1_-cuTrIGiT3xFsWXxM7Z92Hf_Y6Q5zydWhVUzrI0TJgQVjJtZcqslDZwK8O0Qbz5rj_8zD6f6sXRDjnucmGaaHeUjY2ULqqqTvzaJTMEekOoujSZnSznb7eqZ2zeYPyzqQLuLde7ZE9KrnCJvp-ddDIZ1GrMwFIyZwJM5DZ9ZsJ1UoMKAysT3SgEn-JMDFTU34J6S1NtH51mrUZa3CJ1PxYMx34dw1HixsQgTrsDfPwfw75NbrYGLJ3FGXeH7ITVXXL9Y3tEf48sD84Ov1RYa4v-3sQoV4r77cDOg-TskDJG4U24JVDTYuWp66q51HCfgjlK-9h3Gs6L--TbYv716Ji1RRuYE4pfMKuKLHeIyePA9lPWcaUkXOZ5cIVVKvcNAnxZSis8LycSPORQTKT3PC2x8vFDQq0PLtdcBK-9kKG04P6X2lsx1T6AyzUiaccg41ooc6yo8cs0R-pcm8hUA0w1DVONGJGX_TNVBPK4kvopcsPEZNReCphLhozIi4YC5QB82xVtOsN6FRBRa0C5P6CE9euGzd3cMq38qE0G_zIDO2IKzc_6ZnwSY-JWYb1BGplq8D819PZBnJP9yDiIcXDUsxF51U3Sy5f_e9iPru7qY3Ijw3XSRPPsk2sX55vwJFbRGJNd9UONyd67-fLT6bhZfX8AZ_Ixcg
Nature Reviews. Neurology, Volume 16, Issue 12, pp. 706 - 715
Journal Article : Full Text Online
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Prevalence, incidence and carrier frequency of 5q–linked spinal muscular atrophy – a (...)
http://duke.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMwnV1fixMxEA93CuKL-A_d8yxRBEHc6-4m2aRwHPTKFU84PauiPoX8vR602157ffDN7-A39JM4ye4WF8EHYSlsMyndnUxmfsnkNwi9IHmpueODtMhdllKqWSo0y1PNmHZEM1dGxpsv4u234sNEjEc7iLVnYWLSvtGXB9VsflBdTmNu5XJu-m2eWP_8bASYBvwk7e-iXQAwLUSvp1_KSCaa7ctclP112JkLKUMhy4vnaSjQV4iSQ-BedHxRpOz_e2L-wzN1syZrTqnohsZ30Z0mfsTD-n_eQzuuuo9unTU75A_QVeBkUvEk0Wsc1tFjzVCsKouNWoXydNiv6vTp73jhMbv69eNn2MV1Fh9Oj9bLUCULzzd1fioOK-WgiMP-9AiDIFZ4tuVhxvWxl4fo8_jk0-hN2pRVSA0b0OvUeSa4N4UtCLNeG06IDYUNbG6z0kN8xC0xmllWKGXZgAxKR1WeE2E9AbSSkccIa-vMQBDqrLCUOa8BoHthNS2FdQCKEpS1b1aahmw81LyYyQg6RClrvUjQiwx6kSJBr7ZdljXTxr-Ej4O6toKBJDt-sVhdyGaoSJoJR4QrlM8I1eCVqTLCCA03XmmnEvQ8KFsGGowq5NlcqM16LU8_TuQwxKEARUueoJeNkF_AExjVHFtYVC4wZ3Uk9zuSYKem29yOKdnME2sJaLmkEKMSkqBn2-bQM-S-VW6xqWUIoEAOP_GoHoLb525HcoJ4Z3B2Xky3BYwqsog3RrT33z2foNtFNCu46D66cb3auKd1TY0eGOZX3kM3j0_enU96caEDPk-H73vRWH8DDBlBfA
Orphanet Journal Of Rare Diseases, Volume 12, Issue 1, p. 124
Journal Article : Full Text Online
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Spinal muscular atrophy : disease mechanisms and therapy
https://find.library.duke.edu/catalog/DUKE99119256150508501
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Spinal muscular atrophy fact sheet.
https://find.library.duke.edu/catalog/UNCb7031989
Government publication, Web page or site : View Online
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New Hope for Spinal Muscular Atrophy
https://find.library.duke.edu/catalog/DUKE99119497468108501
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